Weekly report: Phase 3 data for JNJ2113, expert discussions, and more
Get caught up with Contemporary Pediatrics! This list helps you navigate our top stories from last week, all in one place.
PODCAST: Auditory brain stem implants in young children.
Jamie Glater, MD, discusses an NIH-sponsored study investigating the effectiveness of an auditory brain stem implant in young children with congenital cochlear nerve agenesis.
Nerivio REN wearable now FDA-cleared to treat migraines in children 8 years and up
With this expanded FDA clearance, the wearable becomes the first FDA-cleared, non-drug therapy to treat acute migraines in children.
FDA approves Kebilidi as first gene therapy to treat aromatic L-amino acid decarboxylase deficiency
With the decision, Kebilidi becomes the first FDA-approved gene therapy for AADC deficiency, and is indicated for adult and pediatric patients.
NGN-401 to treat Rett syndrome demonstrates positive interim data
Data stems from the first 4 patients dosed in a low-dose cohort of an ongoing phase 1/2 open-label trial.
Marinus discontinuing oral ganaxolone trial development to treat seizures in children
The TrustTSC trial did not achieve its primary endpoint of percent reduction in 28-day frequency of TSC-associated seizures.
