FDA approved levacetylleucine (Aqneursa) for ataxia in ataxia-telangiectasia, the first therapy for the disease, in patients 15 kg or heavier.
|Articles|August 16, 2021
What's new on Contemporary Pediatrics: August 16 to 20
A look at what to expect from Contemporary Pediatrics this week
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Seasonal respiratory allergies can make a child's life miserable. There are many available remedies, but which ones are the best options.
The pandemic has led to children spending far less time outdoors and far more time in front of screens, which has led to worries about an increase in myopia. A study from Hong Kong offers some needed information.
Plus, climate change has led to more ferocious weather, increased the risk of wildfires, and led to record breaking temperatures around the globe. What does all of this mean for allergies?
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Tallie Z. Baram, MD, talks about how adding a measure of childhood unpredictability to ACEs screening may help pediatricians identify children at risk for mental health problems.
Review some of the top stories from the Contemporary Pediatrics website over the last week, and catch up on anything you may have missed.
The FDA granted priority review to efzimfotase alfa for HPP in patients aged 2 years and older; a decision is expected in the first half of 2027.
Adolescent VALIANT subgroup data show pegcetacoplan cut proteinuria 75% vs placebo, supporting its expanded pediatric kidney indication.
The FDA approved Fayuvi (rebisufligene etisparvovec-hopf), a one-time AAV9 gene therapy, as the first treatment for pediatric MPS IIIA (Sanfilippo syndrome type A).
Aquestive resubmitted its NDA for dibutepinephrine sublingual film Anaphylm, citing new human factors and PK data addressing the FDA's CRL.
Melissa Wallach, MD, FAAP, discusses what pediatricians should know about updated screening, supplementation, and treatment recommendations for iron deficiency.
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Trending on Contemporary Pediatrics
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Updated AAP guidance changes iron deficiency screening and treatment in children
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FDA approves levacetylleucine as first treatment for ataxia in ataxia-telangiectasia
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FDA grants priority review to efzimfotase alfa for hypophosphatasia in patients aged 2 years and older
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Childhood unpredictability may identify mental health risk missed by ACEs screening
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